2026-04-06T19:06:56Z https://pub.unibl.org/oai

oai:pub.unibl.org:66635 2026-03-17T04:43:22Z

Academic Article text Safety and efficacy of cipaglucosidase alfa plus miglustat versus alglucosidase alfa plus placebo in late-onset Pompe disease(PROPEL): an international randomised,double-blind, parallel-group,phase 3 trial Benedikt Schoser, Mark Roberts, Barry Byrne, Sheela Sitaraman, Hai Jiang, Pascal Laforet, Antonio Toscano, Jeff Castelli, Jordi Diaz- Manera, Mitchell Goldman, Ans T Van der Ploeg, Drago Batkovic, Srilakshimi Kuchipudi, Tahseen Mozaffar, Priya S Kishnani, Agnes Sebok, Alan Pestronk, Александра Доминовић-Ковачевић, Aneal Khan, Blaž Koritnik, Celine Tard, Christopher Lindberg, Collin Quinn, Crystal Eldridge, Cynthia Bodkin, David Reyes-Leiva, Derralynn Hughes, Ela Stefanescu, Emmanuelle Salort-Campana, Ernest Butler, Francoise Bouhour, Gee Kim, George Konstantinos-Papadimas, Giancarlo Parenti, Halina Bartosik-Psujek, Hani Kushlaf, Hashiguchi Akihiro, Heather Lau, Helio Pedro, Henning Andersen, Hernan Amartino, Hideaki Shiraishi, Hiroshi Kobayashi, Ivaylo Tarnev, Jaime Vengoechea, Jennifer Avelar, Jin-Hong Shin, Jonathan Cauci, Jorge Alonso-Perez, Jozsef Janszky, Julie Berthy, Cornelia Kornblum, Kristina Gutschmidt, Kristl Claeys, Maria Judit-Molnar, Marie Wencel, Mark Tarnopolsky, Mazen Dimachkie, Michel Tchan, Miriam Freimer, Nikola Longo, Nuria Vidal-Fernandez, Olimpia Musumeci, Ozlem Goker-Alpan, Patrick Deegan, Paula Clemens, Richard Roxburgh, Robert Henderson, Robert Hopkin, Sabrina Sacconi, Simona Fecarotta, Shahram Attarian, Stephan Wenninger, Stephanie Dearmey, Tarekegn Hiwot, Thomas Burrow, Tobias Ruck, Tomo Sawada, Vescei Laszlo, Wolfgang Loscher, Yin-Hsiu Chien Benedikt Schoser Unknown Mark Roberts Unknown Barry Byrne Unknown Sheela Sitaraman Unknown Hai Jiang Unknown Pascal Laforet Unknown Antonio Toscano Unknown Jeff Castelli Unknown Jordi Diaz- Manera Unknown Mitchell Goldman Unknown Ans T Van der Ploeg Unknown Drago Batkovic Unknown Srilakshimi Kuchipudi Unknown Tahseen Mozaffar Unknown Priya S Kishnani Unknown Agnes Sebok Unknown Alan Pestronk Unknown Александра Доминовић-Ковачевић Unknown Aneal Khan Unknown Blaž Koritnik Unknown Celine Tard Unknown Christopher Lindberg Unknown Collin Quinn Unknown Crystal Eldridge Unknown Cynthia Bodkin Unknown David Reyes-Leiva Unknown Derralynn Hughes Unknown Ela Stefanescu Unknown Emmanuelle Salort-Campana Unknown Ernest Butler Unknown Francoise Bouhour Unknown Gee Kim Unknown George Konstantinos-Papadimas Unknown Giancarlo Parenti Unknown Halina Bartosik-Psujek Unknown Hani Kushlaf Unknown Hashiguchi Akihiro Unknown Heather Lau Unknown Helio Pedro Unknown Henning Andersen Unknown Hernan Amartino Unknown Hideaki Shiraishi Unknown Hiroshi Kobayashi Unknown Ivaylo Tarnev Unknown Jaime Vengoechea Unknown Jennifer Avelar Unknown Jin-Hong Shin Unknown Jonathan Cauci Unknown Jorge Alonso-Perez Unknown Jozsef Janszky Unknown Julie Berthy Unknown Cornelia Kornblum Unknown Kristina Gutschmidt Unknown Kristl Claeys Unknown Maria Judit-Molnar Unknown Marie Wencel Unknown Mark Tarnopolsky Unknown Mazen Dimachkie Unknown Michel Tchan Unknown Miriam Freimer Unknown Nikola Longo Unknown Nuria Vidal-Fernandez Unknown Olimpia Musumeci Unknown Ozlem Goker-Alpan Unknown Patrick Deegan Unknown Paula Clemens Unknown Richard Roxburgh Unknown Robert Henderson Unknown Robert Hopkin Unknown Sabrina Sacconi Unknown Simona Fecarotta Unknown Shahram Attarian Unknown Stephan Wenninger Unknown Stephanie Dearmey Unknown Tarekegn Hiwot Unknown Thomas Burrow Unknown Tobias Ruck Unknown Tomo Sawada Unknown Vescei Laszlo Unknown Wolfgang Loscher Unknown Yin-Hsiu Chien Unknown not applicable 2021-12 2021-12 2021-12 location unknown 66635 item oai:pub.unibl.org:66635