2026-04-06T20:30:23Z
https://pub.unibl.org/oai
oai:pub.unibl.org:66635
2026-03-17T04:43:22Z
Safety and efficacy of cipaglucosidase alfa plus miglustat versus alglucosidase alfa plus placebo in late-onset Pompe disease(PROPEL): an international randomised,double-blind, parallel-group,phase 3 trial
Benedikt Schoser
creator
Mark Roberts
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Barry Byrne
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Sheela Sitaraman
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Hai Jiang
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Pascal Laforet
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Antonio Toscano
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Jeff Castelli
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Jordi Diaz- Manera
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Mitchell Goldman
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Ans T Van der Ploeg
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Drago Batkovic
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Srilakshimi Kuchipudi
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Tahseen Mozaffar
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Priya S Kishnani
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Agnes Sebok
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Alan Pestronk
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Александра Доминовић-Ковачевић
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Aneal Khan
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Blaž Koritnik
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Celine Tard
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Christopher Lindberg
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Collin Quinn
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Crystal Eldridge
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Cynthia Bodkin
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David Reyes-Leiva
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Derralynn Hughes
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Ela Stefanescu
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Emmanuelle Salort-Campana
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Ernest Butler
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Francoise Bouhour
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Gee Kim
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George Konstantinos-Papadimas
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Giancarlo Parenti
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Halina Bartosik-Psujek
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Hani Kushlaf
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Hashiguchi Akihiro
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Heather Lau
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Helio Pedro
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Henning Andersen
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Hernan Amartino
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Hideaki Shiraishi
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Hiroshi Kobayashi
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Ivaylo Tarnev
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Jaime Vengoechea
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Jennifer Avelar
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Jin-Hong Shin
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Jonathan Cauci
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Jorge Alonso-Perez
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Jozsef Janszky
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Julie Berthy
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Cornelia Kornblum
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Kristina Gutschmidt
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Kristl Claeys
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Maria Judit-Molnar
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Marie Wencel
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Mark Tarnopolsky
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Mazen Dimachkie
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Michel Tchan
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Miriam Freimer
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Nikola Longo
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Nuria Vidal-Fernandez
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Olimpia Musumeci
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Ozlem Goker-Alpan
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Patrick Deegan
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Paula Clemens
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Richard Roxburgh
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Robert Henderson
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Robert Hopkin
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Sabrina Sacconi
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Simona Fecarotta
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Shahram Attarian
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Stephan Wenninger
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Stephanie Dearmey
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Tarekegn Hiwot
creator
Thomas Burrow
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Tobias Ruck
creator
Tomo Sawada
creator
Vescei Laszlo
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Wolfgang Loscher
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Yin-Hsiu Chien
creator
Academic Article
text
/unibl/sci/idNaucniRad:37266
THE LANCET NEUROLOGY
1474-4422
https://pub.unibl.org/s/cir/item/66635
2021-12
66635