2026-04-06T20:32:13Z https://pub.unibl.org/oai

oai:pub.unibl.org:66635 2026-03-17T04:43:22Z

Safety and efficacy of cipaglucosidase alfa plus miglustat versus alglucosidase alfa plus placebo in late-onset Pompe disease(PROPEL): an international randomised,double-blind, parallel-group,phase 3 trial /unibl/author/Benedikt Schoser /unibl/author/Mark Roberts /unibl/author/Barry Byrne /unibl/author/Sheela Sitaraman /unibl/author/Hai Jiang /unibl/author/Pascal Laforet /unibl/author/Antonio Toscano /unibl/author/Jeff Castelli /unibl/author/Jordi Diaz- Manera /unibl/author/Mitchell Goldman /unibl/author/Ans T Van der Ploeg /unibl/author/Drago Batkovic /unibl/author/Srilakshimi Kuchipudi /unibl/author/Tahseen Mozaffar /unibl/author/Priya S Kishnani /unibl/author/Agnes Sebok /unibl/author/Alan Pestronk https://www.unibl.org/sr-lat/fis/zaposlen/3327-aleksandra-dominovic-kovacevic /unibl/author/Aneal Khan /unibl/author/Blaž Koritnik /unibl/author/Celine Tard /unibl/author/Christopher Lindberg /unibl/author/Collin Quinn /unibl/author/Crystal Eldridge /unibl/author/Cynthia Bodkin /unibl/author/David Reyes-Leiva /unibl/author/Derralynn Hughes /unibl/author/Ela Stefanescu /unibl/author/Emmanuelle Salort-Campana /unibl/author/Ernest Butler /unibl/author/Francoise Bouhour /unibl/author/Gee Kim /unibl/author/George Konstantinos-Papadimas /unibl/author/Giancarlo Parenti /unibl/author/Halina Bartosik-Psujek /unibl/author/Hani Kushlaf /unibl/author/Hashiguchi Akihiro /unibl/author/Heather Lau /unibl/author/Helio Pedro /unibl/author/Henning Andersen /unibl/author/Hernan Amartino /unibl/author/Hideaki Shiraishi /unibl/author/Hiroshi Kobayashi /unibl/author/Ivaylo Tarnev /unibl/author/Jaime Vengoechea /unibl/author/Jennifer Avelar /unibl/author/Jin-Hong Shin /unibl/author/Jonathan Cauci /unibl/author/Jorge Alonso-Perez /unibl/author/Jozsef Janszky /unibl/author/Julie Berthy /unibl/author/Cornelia Kornblum /unibl/author/Kristina Gutschmidt /unibl/author/Kristl Claeys /unibl/author/Maria Judit-Molnar /unibl/author/Marie Wencel /unibl/author/Mark Tarnopolsky /unibl/author/Mazen Dimachkie /unibl/author/Michel Tchan /unibl/author/Miriam Freimer /unibl/author/Nikola Longo /unibl/author/Nuria Vidal-Fernandez /unibl/author/Olimpia Musumeci /unibl/author/Ozlem Goker-Alpan /unibl/author/Patrick Deegan /unibl/author/Paula Clemens /unibl/author/Richard Roxburgh /unibl/author/Robert Henderson /unibl/author/Robert Hopkin /unibl/author/Sabrina Sacconi /unibl/author/Simona Fecarotta /unibl/author/Shahram Attarian /unibl/author/Stephan Wenninger /unibl/author/Stephanie Dearmey /unibl/author/Tarekegn Hiwot /unibl/author/Thomas Burrow /unibl/author/Tobias Ruck /unibl/author/Tomo Sawada /unibl/author/Vescei Laszlo /unibl/author/Wolfgang Loscher /unibl/author/Yin-Hsiu Chien 2021-12 Academic Article text 1037 1027 /unibl/sci/idNaucniRad:37266 THE LANCET NEUROLOGY 1474-4422 https://pub.unibl.org/s/cir/item/66635